Efficient Precision Genome Editing in iPSCs via Genetic Co-targeting with Selection
Genome editing in induced pluripotent stem cells is currently hampered by the laborious and expensive nature of identifying homology-directed repair (HDR)-modified cells. We present an approach where isolation of cells bearing a selectable, HDR-mediated editing event at one locus enriches for HDR-me...
Ausführliche Beschreibung
Autor*in: |
Katie A. Mitzelfelt [verfasserIn] Chris McDermott-Roe [verfasserIn] Michael N. Grzybowski [verfasserIn] Maribel Marquez [verfasserIn] Chieh-Ti Kuo [verfasserIn] Michael Riedel [verfasserIn] Shuping Lai [verfasserIn] Melinda J. Choi [verfasserIn] Kurt D. Kolander [verfasserIn] Daniel Helbling [verfasserIn] David P. Dimmock [verfasserIn] Michele A. Battle [verfasserIn] Chuanchau J. Jou [verfasserIn] Martin Tristani-Firouzi [verfasserIn] James W. Verbsky [verfasserIn] Ivor J. Benjamin [verfasserIn] Aron M. Geurts [verfasserIn] |
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Format: |
E-Artikel |
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Sprache: |
Englisch |
Erschienen: |
2017 |
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Übergeordnetes Werk: |
In: Stem Cell Reports - Elsevier, 2015, 8(2017), 3, Seite 491-499 |
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Übergeordnetes Werk: |
volume:8 ; year:2017 ; number:3 ; pages:491-499 |
Links: |
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DOI / URN: |
10.1016/j.stemcr.2017.01.021 |
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Katalog-ID: |
DOAJ074869795 |
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10.1016/j.stemcr.2017.01.021 doi (DE-627)DOAJ074869795 (DE-599)DOAJ83b03a2018cb4c5d8fd10a28c1724404 DE-627 ger DE-627 rakwb eng R5-920 QH301-705.5 Katie A. Mitzelfelt verfasserin aut Efficient Precision Genome Editing in iPSCs via Genetic Co-targeting with Selection 2017 Text txt rdacontent Computermedien c rdamedia Online-Ressource cr rdacarrier Genome editing in induced pluripotent stem cells is currently hampered by the laborious and expensive nature of identifying homology-directed repair (HDR)-modified cells. We present an approach where isolation of cells bearing a selectable, HDR-mediated editing event at one locus enriches for HDR-mediated edits at additional loci. This strategy, called co-targeting with selection, improves the probability of isolating cells bearing HDR-mediated variants and accelerates the production of disease models. Medicine (General) Biology (General) Chris McDermott-Roe verfasserin aut Michael N. Grzybowski verfasserin aut Maribel Marquez verfasserin aut Chieh-Ti Kuo verfasserin aut Michael Riedel verfasserin aut Shuping Lai verfasserin aut Melinda J. Choi verfasserin aut Kurt D. Kolander verfasserin aut Daniel Helbling verfasserin aut David P. Dimmock verfasserin aut Michele A. Battle verfasserin aut Chuanchau J. Jou verfasserin aut Martin Tristani-Firouzi verfasserin aut James W. Verbsky verfasserin aut Ivor J. Benjamin verfasserin aut Aron M. Geurts verfasserin aut In Stem Cell Reports Elsevier, 2015 8(2017), 3, Seite 491-499 (DE-627)749730862 (DE-600)2720528-9 22136711 nnns volume:8 year:2017 number:3 pages:491-499 https://doi.org/10.1016/j.stemcr.2017.01.021 kostenfrei https://doaj.org/article/83b03a2018cb4c5d8fd10a28c1724404 kostenfrei http://www.sciencedirect.com/science/article/pii/S2213671117300371 kostenfrei https://doaj.org/toc/2213-6711 Journal toc kostenfrei GBV_USEFLAG_A SYSFLAG_A GBV_DOAJ GBV_ILN_20 GBV_ILN_22 GBV_ILN_23 GBV_ILN_24 GBV_ILN_31 GBV_ILN_39 GBV_ILN_40 GBV_ILN_60 GBV_ILN_62 GBV_ILN_63 GBV_ILN_65 GBV_ILN_69 GBV_ILN_73 GBV_ILN_74 GBV_ILN_95 GBV_ILN_105 GBV_ILN_110 GBV_ILN_151 GBV_ILN_161 GBV_ILN_170 GBV_ILN_206 GBV_ILN_213 GBV_ILN_230 GBV_ILN_285 GBV_ILN_293 GBV_ILN_602 GBV_ILN_2001 GBV_ILN_2003 GBV_ILN_2005 GBV_ILN_2006 GBV_ILN_2007 GBV_ILN_2008 GBV_ILN_2009 GBV_ILN_2010 GBV_ILN_2011 GBV_ILN_2014 GBV_ILN_2015 GBV_ILN_2020 GBV_ILN_2021 GBV_ILN_2025 GBV_ILN_2026 GBV_ILN_2027 GBV_ILN_2038 GBV_ILN_2044 GBV_ILN_2048 GBV_ILN_2049 GBV_ILN_2050 GBV_ILN_2055 GBV_ILN_2059 GBV_ILN_2061 GBV_ILN_2064 GBV_ILN_2068 GBV_ILN_2088 GBV_ILN_2110 GBV_ILN_2112 GBV_ILN_2129 GBV_ILN_2143 GBV_ILN_2153 GBV_ILN_2190 GBV_ILN_2336 GBV_ILN_2470 GBV_ILN_2507 GBV_ILN_4012 GBV_ILN_4035 GBV_ILN_4037 GBV_ILN_4112 GBV_ILN_4125 GBV_ILN_4126 GBV_ILN_4249 GBV_ILN_4251 GBV_ILN_4305 GBV_ILN_4306 GBV_ILN_4307 GBV_ILN_4313 GBV_ILN_4322 GBV_ILN_4323 GBV_ILN_4324 GBV_ILN_4325 GBV_ILN_4326 GBV_ILN_4333 GBV_ILN_4338 GBV_ILN_4367 GBV_ILN_4393 GBV_ILN_4700 AR 8 2017 3 491-499 |
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10.1016/j.stemcr.2017.01.021 doi (DE-627)DOAJ074869795 (DE-599)DOAJ83b03a2018cb4c5d8fd10a28c1724404 DE-627 ger DE-627 rakwb eng R5-920 QH301-705.5 Katie A. Mitzelfelt verfasserin aut Efficient Precision Genome Editing in iPSCs via Genetic Co-targeting with Selection 2017 Text txt rdacontent Computermedien c rdamedia Online-Ressource cr rdacarrier Genome editing in induced pluripotent stem cells is currently hampered by the laborious and expensive nature of identifying homology-directed repair (HDR)-modified cells. We present an approach where isolation of cells bearing a selectable, HDR-mediated editing event at one locus enriches for HDR-mediated edits at additional loci. This strategy, called co-targeting with selection, improves the probability of isolating cells bearing HDR-mediated variants and accelerates the production of disease models. Medicine (General) Biology (General) Chris McDermott-Roe verfasserin aut Michael N. Grzybowski verfasserin aut Maribel Marquez verfasserin aut Chieh-Ti Kuo verfasserin aut Michael Riedel verfasserin aut Shuping Lai verfasserin aut Melinda J. Choi verfasserin aut Kurt D. Kolander verfasserin aut Daniel Helbling verfasserin aut David P. Dimmock verfasserin aut Michele A. Battle verfasserin aut Chuanchau J. Jou verfasserin aut Martin Tristani-Firouzi verfasserin aut James W. Verbsky verfasserin aut Ivor J. Benjamin verfasserin aut Aron M. Geurts verfasserin aut In Stem Cell Reports Elsevier, 2015 8(2017), 3, Seite 491-499 (DE-627)749730862 (DE-600)2720528-9 22136711 nnns volume:8 year:2017 number:3 pages:491-499 https://doi.org/10.1016/j.stemcr.2017.01.021 kostenfrei https://doaj.org/article/83b03a2018cb4c5d8fd10a28c1724404 kostenfrei http://www.sciencedirect.com/science/article/pii/S2213671117300371 kostenfrei https://doaj.org/toc/2213-6711 Journal toc kostenfrei GBV_USEFLAG_A SYSFLAG_A GBV_DOAJ GBV_ILN_20 GBV_ILN_22 GBV_ILN_23 GBV_ILN_24 GBV_ILN_31 GBV_ILN_39 GBV_ILN_40 GBV_ILN_60 GBV_ILN_62 GBV_ILN_63 GBV_ILN_65 GBV_ILN_69 GBV_ILN_73 GBV_ILN_74 GBV_ILN_95 GBV_ILN_105 GBV_ILN_110 GBV_ILN_151 GBV_ILN_161 GBV_ILN_170 GBV_ILN_206 GBV_ILN_213 GBV_ILN_230 GBV_ILN_285 GBV_ILN_293 GBV_ILN_602 GBV_ILN_2001 GBV_ILN_2003 GBV_ILN_2005 GBV_ILN_2006 GBV_ILN_2007 GBV_ILN_2008 GBV_ILN_2009 GBV_ILN_2010 GBV_ILN_2011 GBV_ILN_2014 GBV_ILN_2015 GBV_ILN_2020 GBV_ILN_2021 GBV_ILN_2025 GBV_ILN_2026 GBV_ILN_2027 GBV_ILN_2038 GBV_ILN_2044 GBV_ILN_2048 GBV_ILN_2049 GBV_ILN_2050 GBV_ILN_2055 GBV_ILN_2059 GBV_ILN_2061 GBV_ILN_2064 GBV_ILN_2068 GBV_ILN_2088 GBV_ILN_2110 GBV_ILN_2112 GBV_ILN_2129 GBV_ILN_2143 GBV_ILN_2153 GBV_ILN_2190 GBV_ILN_2336 GBV_ILN_2470 GBV_ILN_2507 GBV_ILN_4012 GBV_ILN_4035 GBV_ILN_4037 GBV_ILN_4112 GBV_ILN_4125 GBV_ILN_4126 GBV_ILN_4249 GBV_ILN_4251 GBV_ILN_4305 GBV_ILN_4306 GBV_ILN_4307 GBV_ILN_4313 GBV_ILN_4322 GBV_ILN_4323 GBV_ILN_4324 GBV_ILN_4325 GBV_ILN_4326 GBV_ILN_4333 GBV_ILN_4338 GBV_ILN_4367 GBV_ILN_4393 GBV_ILN_4700 AR 8 2017 3 491-499 |
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10.1016/j.stemcr.2017.01.021 doi (DE-627)DOAJ074869795 (DE-599)DOAJ83b03a2018cb4c5d8fd10a28c1724404 DE-627 ger DE-627 rakwb eng R5-920 QH301-705.5 Katie A. Mitzelfelt verfasserin aut Efficient Precision Genome Editing in iPSCs via Genetic Co-targeting with Selection 2017 Text txt rdacontent Computermedien c rdamedia Online-Ressource cr rdacarrier Genome editing in induced pluripotent stem cells is currently hampered by the laborious and expensive nature of identifying homology-directed repair (HDR)-modified cells. We present an approach where isolation of cells bearing a selectable, HDR-mediated editing event at one locus enriches for HDR-mediated edits at additional loci. This strategy, called co-targeting with selection, improves the probability of isolating cells bearing HDR-mediated variants and accelerates the production of disease models. Medicine (General) Biology (General) Chris McDermott-Roe verfasserin aut Michael N. Grzybowski verfasserin aut Maribel Marquez verfasserin aut Chieh-Ti Kuo verfasserin aut Michael Riedel verfasserin aut Shuping Lai verfasserin aut Melinda J. Choi verfasserin aut Kurt D. Kolander verfasserin aut Daniel Helbling verfasserin aut David P. Dimmock verfasserin aut Michele A. Battle verfasserin aut Chuanchau J. Jou verfasserin aut Martin Tristani-Firouzi verfasserin aut James W. Verbsky verfasserin aut Ivor J. Benjamin verfasserin aut Aron M. Geurts verfasserin aut In Stem Cell Reports Elsevier, 2015 8(2017), 3, Seite 491-499 (DE-627)749730862 (DE-600)2720528-9 22136711 nnns volume:8 year:2017 number:3 pages:491-499 https://doi.org/10.1016/j.stemcr.2017.01.021 kostenfrei https://doaj.org/article/83b03a2018cb4c5d8fd10a28c1724404 kostenfrei http://www.sciencedirect.com/science/article/pii/S2213671117300371 kostenfrei https://doaj.org/toc/2213-6711 Journal toc kostenfrei GBV_USEFLAG_A SYSFLAG_A GBV_DOAJ GBV_ILN_20 GBV_ILN_22 GBV_ILN_23 GBV_ILN_24 GBV_ILN_31 GBV_ILN_39 GBV_ILN_40 GBV_ILN_60 GBV_ILN_62 GBV_ILN_63 GBV_ILN_65 GBV_ILN_69 GBV_ILN_73 GBV_ILN_74 GBV_ILN_95 GBV_ILN_105 GBV_ILN_110 GBV_ILN_151 GBV_ILN_161 GBV_ILN_170 GBV_ILN_206 GBV_ILN_213 GBV_ILN_230 GBV_ILN_285 GBV_ILN_293 GBV_ILN_602 GBV_ILN_2001 GBV_ILN_2003 GBV_ILN_2005 GBV_ILN_2006 GBV_ILN_2007 GBV_ILN_2008 GBV_ILN_2009 GBV_ILN_2010 GBV_ILN_2011 GBV_ILN_2014 GBV_ILN_2015 GBV_ILN_2020 GBV_ILN_2021 GBV_ILN_2025 GBV_ILN_2026 GBV_ILN_2027 GBV_ILN_2038 GBV_ILN_2044 GBV_ILN_2048 GBV_ILN_2049 GBV_ILN_2050 GBV_ILN_2055 GBV_ILN_2059 GBV_ILN_2061 GBV_ILN_2064 GBV_ILN_2068 GBV_ILN_2088 GBV_ILN_2110 GBV_ILN_2112 GBV_ILN_2129 GBV_ILN_2143 GBV_ILN_2153 GBV_ILN_2190 GBV_ILN_2336 GBV_ILN_2470 GBV_ILN_2507 GBV_ILN_4012 GBV_ILN_4035 GBV_ILN_4037 GBV_ILN_4112 GBV_ILN_4125 GBV_ILN_4126 GBV_ILN_4249 GBV_ILN_4251 GBV_ILN_4305 GBV_ILN_4306 GBV_ILN_4307 GBV_ILN_4313 GBV_ILN_4322 GBV_ILN_4323 GBV_ILN_4324 GBV_ILN_4325 GBV_ILN_4326 GBV_ILN_4333 GBV_ILN_4338 GBV_ILN_4367 GBV_ILN_4393 GBV_ILN_4700 AR 8 2017 3 491-499 |
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10.1016/j.stemcr.2017.01.021 doi (DE-627)DOAJ074869795 (DE-599)DOAJ83b03a2018cb4c5d8fd10a28c1724404 DE-627 ger DE-627 rakwb eng R5-920 QH301-705.5 Katie A. Mitzelfelt verfasserin aut Efficient Precision Genome Editing in iPSCs via Genetic Co-targeting with Selection 2017 Text txt rdacontent Computermedien c rdamedia Online-Ressource cr rdacarrier Genome editing in induced pluripotent stem cells is currently hampered by the laborious and expensive nature of identifying homology-directed repair (HDR)-modified cells. We present an approach where isolation of cells bearing a selectable, HDR-mediated editing event at one locus enriches for HDR-mediated edits at additional loci. This strategy, called co-targeting with selection, improves the probability of isolating cells bearing HDR-mediated variants and accelerates the production of disease models. Medicine (General) Biology (General) Chris McDermott-Roe verfasserin aut Michael N. Grzybowski verfasserin aut Maribel Marquez verfasserin aut Chieh-Ti Kuo verfasserin aut Michael Riedel verfasserin aut Shuping Lai verfasserin aut Melinda J. Choi verfasserin aut Kurt D. Kolander verfasserin aut Daniel Helbling verfasserin aut David P. Dimmock verfasserin aut Michele A. Battle verfasserin aut Chuanchau J. Jou verfasserin aut Martin Tristani-Firouzi verfasserin aut James W. Verbsky verfasserin aut Ivor J. Benjamin verfasserin aut Aron M. Geurts verfasserin aut In Stem Cell Reports Elsevier, 2015 8(2017), 3, Seite 491-499 (DE-627)749730862 (DE-600)2720528-9 22136711 nnns volume:8 year:2017 number:3 pages:491-499 https://doi.org/10.1016/j.stemcr.2017.01.021 kostenfrei https://doaj.org/article/83b03a2018cb4c5d8fd10a28c1724404 kostenfrei http://www.sciencedirect.com/science/article/pii/S2213671117300371 kostenfrei https://doaj.org/toc/2213-6711 Journal toc kostenfrei GBV_USEFLAG_A SYSFLAG_A GBV_DOAJ GBV_ILN_20 GBV_ILN_22 GBV_ILN_23 GBV_ILN_24 GBV_ILN_31 GBV_ILN_39 GBV_ILN_40 GBV_ILN_60 GBV_ILN_62 GBV_ILN_63 GBV_ILN_65 GBV_ILN_69 GBV_ILN_73 GBV_ILN_74 GBV_ILN_95 GBV_ILN_105 GBV_ILN_110 GBV_ILN_151 GBV_ILN_161 GBV_ILN_170 GBV_ILN_206 GBV_ILN_213 GBV_ILN_230 GBV_ILN_285 GBV_ILN_293 GBV_ILN_602 GBV_ILN_2001 GBV_ILN_2003 GBV_ILN_2005 GBV_ILN_2006 GBV_ILN_2007 GBV_ILN_2008 GBV_ILN_2009 GBV_ILN_2010 GBV_ILN_2011 GBV_ILN_2014 GBV_ILN_2015 GBV_ILN_2020 GBV_ILN_2021 GBV_ILN_2025 GBV_ILN_2026 GBV_ILN_2027 GBV_ILN_2038 GBV_ILN_2044 GBV_ILN_2048 GBV_ILN_2049 GBV_ILN_2050 GBV_ILN_2055 GBV_ILN_2059 GBV_ILN_2061 GBV_ILN_2064 GBV_ILN_2068 GBV_ILN_2088 GBV_ILN_2110 GBV_ILN_2112 GBV_ILN_2129 GBV_ILN_2143 GBV_ILN_2153 GBV_ILN_2190 GBV_ILN_2336 GBV_ILN_2470 GBV_ILN_2507 GBV_ILN_4012 GBV_ILN_4035 GBV_ILN_4037 GBV_ILN_4112 GBV_ILN_4125 GBV_ILN_4126 GBV_ILN_4249 GBV_ILN_4251 GBV_ILN_4305 GBV_ILN_4306 GBV_ILN_4307 GBV_ILN_4313 GBV_ILN_4322 GBV_ILN_4323 GBV_ILN_4324 GBV_ILN_4325 GBV_ILN_4326 GBV_ILN_4333 GBV_ILN_4338 GBV_ILN_4367 GBV_ILN_4393 GBV_ILN_4700 AR 8 2017 3 491-499 |
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10.1016/j.stemcr.2017.01.021 doi (DE-627)DOAJ074869795 (DE-599)DOAJ83b03a2018cb4c5d8fd10a28c1724404 DE-627 ger DE-627 rakwb eng R5-920 QH301-705.5 Katie A. Mitzelfelt verfasserin aut Efficient Precision Genome Editing in iPSCs via Genetic Co-targeting with Selection 2017 Text txt rdacontent Computermedien c rdamedia Online-Ressource cr rdacarrier Genome editing in induced pluripotent stem cells is currently hampered by the laborious and expensive nature of identifying homology-directed repair (HDR)-modified cells. We present an approach where isolation of cells bearing a selectable, HDR-mediated editing event at one locus enriches for HDR-mediated edits at additional loci. This strategy, called co-targeting with selection, improves the probability of isolating cells bearing HDR-mediated variants and accelerates the production of disease models. Medicine (General) Biology (General) Chris McDermott-Roe verfasserin aut Michael N. Grzybowski verfasserin aut Maribel Marquez verfasserin aut Chieh-Ti Kuo verfasserin aut Michael Riedel verfasserin aut Shuping Lai verfasserin aut Melinda J. Choi verfasserin aut Kurt D. Kolander verfasserin aut Daniel Helbling verfasserin aut David P. Dimmock verfasserin aut Michele A. Battle verfasserin aut Chuanchau J. Jou verfasserin aut Martin Tristani-Firouzi verfasserin aut James W. Verbsky verfasserin aut Ivor J. Benjamin verfasserin aut Aron M. Geurts verfasserin aut In Stem Cell Reports Elsevier, 2015 8(2017), 3, Seite 491-499 (DE-627)749730862 (DE-600)2720528-9 22136711 nnns volume:8 year:2017 number:3 pages:491-499 https://doi.org/10.1016/j.stemcr.2017.01.021 kostenfrei https://doaj.org/article/83b03a2018cb4c5d8fd10a28c1724404 kostenfrei http://www.sciencedirect.com/science/article/pii/S2213671117300371 kostenfrei https://doaj.org/toc/2213-6711 Journal toc kostenfrei GBV_USEFLAG_A SYSFLAG_A GBV_DOAJ GBV_ILN_20 GBV_ILN_22 GBV_ILN_23 GBV_ILN_24 GBV_ILN_31 GBV_ILN_39 GBV_ILN_40 GBV_ILN_60 GBV_ILN_62 GBV_ILN_63 GBV_ILN_65 GBV_ILN_69 GBV_ILN_73 GBV_ILN_74 GBV_ILN_95 GBV_ILN_105 GBV_ILN_110 GBV_ILN_151 GBV_ILN_161 GBV_ILN_170 GBV_ILN_206 GBV_ILN_213 GBV_ILN_230 GBV_ILN_285 GBV_ILN_293 GBV_ILN_602 GBV_ILN_2001 GBV_ILN_2003 GBV_ILN_2005 GBV_ILN_2006 GBV_ILN_2007 GBV_ILN_2008 GBV_ILN_2009 GBV_ILN_2010 GBV_ILN_2011 GBV_ILN_2014 GBV_ILN_2015 GBV_ILN_2020 GBV_ILN_2021 GBV_ILN_2025 GBV_ILN_2026 GBV_ILN_2027 GBV_ILN_2038 GBV_ILN_2044 GBV_ILN_2048 GBV_ILN_2049 GBV_ILN_2050 GBV_ILN_2055 GBV_ILN_2059 GBV_ILN_2061 GBV_ILN_2064 GBV_ILN_2068 GBV_ILN_2088 GBV_ILN_2110 GBV_ILN_2112 GBV_ILN_2129 GBV_ILN_2143 GBV_ILN_2153 GBV_ILN_2190 GBV_ILN_2336 GBV_ILN_2470 GBV_ILN_2507 GBV_ILN_4012 GBV_ILN_4035 GBV_ILN_4037 GBV_ILN_4112 GBV_ILN_4125 GBV_ILN_4126 GBV_ILN_4249 GBV_ILN_4251 GBV_ILN_4305 GBV_ILN_4306 GBV_ILN_4307 GBV_ILN_4313 GBV_ILN_4322 GBV_ILN_4323 GBV_ILN_4324 GBV_ILN_4325 GBV_ILN_4326 GBV_ILN_4333 GBV_ILN_4338 GBV_ILN_4367 GBV_ILN_4393 GBV_ILN_4700 AR 8 2017 3 491-499 |
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Katie A. Mitzelfelt @@aut@@ Chris McDermott-Roe @@aut@@ Michael N. Grzybowski @@aut@@ Maribel Marquez @@aut@@ Chieh-Ti Kuo @@aut@@ Michael Riedel @@aut@@ Shuping Lai @@aut@@ Melinda J. Choi @@aut@@ Kurt D. Kolander @@aut@@ Daniel Helbling @@aut@@ David P. Dimmock @@aut@@ Michele A. Battle @@aut@@ Chuanchau J. Jou @@aut@@ Martin Tristani-Firouzi @@aut@@ James W. Verbsky @@aut@@ Ivor J. Benjamin @@aut@@ Aron M. Geurts @@aut@@ |
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Efficient Precision Genome Editing in iPSCs via Genetic Co-targeting with Selection |
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Genome editing in induced pluripotent stem cells is currently hampered by the laborious and expensive nature of identifying homology-directed repair (HDR)-modified cells. We present an approach where isolation of cells bearing a selectable, HDR-mediated editing event at one locus enriches for HDR-mediated edits at additional loci. This strategy, called co-targeting with selection, improves the probability of isolating cells bearing HDR-mediated variants and accelerates the production of disease models. |
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Genome editing in induced pluripotent stem cells is currently hampered by the laborious and expensive nature of identifying homology-directed repair (HDR)-modified cells. We present an approach where isolation of cells bearing a selectable, HDR-mediated editing event at one locus enriches for HDR-mediated edits at additional loci. This strategy, called co-targeting with selection, improves the probability of isolating cells bearing HDR-mediated variants and accelerates the production of disease models. |
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Genome editing in induced pluripotent stem cells is currently hampered by the laborious and expensive nature of identifying homology-directed repair (HDR)-modified cells. We present an approach where isolation of cells bearing a selectable, HDR-mediated editing event at one locus enriches for HDR-mediated edits at additional loci. This strategy, called co-targeting with selection, improves the probability of isolating cells bearing HDR-mediated variants and accelerates the production of disease models. |
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Efficient Precision Genome Editing in iPSCs via Genetic Co-targeting with Selection |
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|
score |
7.401017 |