P006: Long-term safety and efficacy of pegunigalsidase alfa administered every 4 weeks in Fabry disease: 2-Year interim results from BRIGHT51
Autor*in: |
John Bernat [verfasserIn] Myrl Holida [verfasserIn] Nicola Longo [verfasserIn] Ozlem Goker-Alpan [verfasserIn] Eric Wallace [verfasserIn] Patrick Deegan [verfasserIn] Camilla Tondel [verfasserIn] Francois Eyskens [verfasserIn] Ulla Feldt-Rasmussen [verfasserIn] Derralynn Hughes [verfasserIn] Antonio Pisani [verfasserIn] Ales Linhart [verfasserIn] Rossana Rocco [verfasserIn] Einat Almon [verfasserIn] Sari Alon [verfasserIn] Raul Chertkoff [verfasserIn] David Warnock [verfasserIn] Stephen Waldek [verfasserIn] William Wilcox [verfasserIn] |
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Format: |
E-Artikel |
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Sprache: |
Englisch |
Erschienen: |
2023 |
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Übergeordnetes Werk: |
In: Genetics in Medicine Open ; 1(2023), 1, Seite 100016- volume:1 ; year:2023 ; number:1 ; pages:100016- |
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Links: |
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DOI / URN: |
10.1016/j.gimo.2023.100016 |
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Katalog-ID: |
DOAJ096280204 |
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QH - Natural History and Biology |
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up_date |
2024-07-03T19:16:54.923Z |
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