Lentiviral hematopoietic stem and progenitor cell gene therapy (HSPC-GT) for metachromatic leukodystrophy (MLD): Clinical outcomes from 33 patients
Autor*in: |
Fumagalli, Francesca [verfasserIn] |
---|
Format: |
E-Artikel |
---|---|
Sprache: |
Englisch |
Erschienen: |
2020 |
---|
Übergeordnetes Werk: |
Enthalten in: Measles transmission during a large outbreak in California - Worden, Lee ELSEVIER, 2019, Orlando, Fla |
---|---|
Übergeordnetes Werk: |
volume:129 ; year:2020 ; number:2 ; pages:59 |
Links: |
---|
DOI / URN: |
10.1016/j.ymgme.2019.11.135 |
---|
Katalog-ID: |
ELV049242695 |
---|
LEADER | 01000caa a22002652 4500 | ||
---|---|---|---|
001 | ELV049242695 | ||
003 | DE-627 | ||
005 | 20230624152937.0 | ||
007 | cr uuu---uuuuu | ||
008 | 200518s2020 xx |||||o 00| ||eng c | ||
024 | 7 | |a 10.1016/j.ymgme.2019.11.135 |2 doi | |
028 | 5 | 2 | |a /cbs_pica/cbs_olc/import_discovery/elsevier/einzuspielen/GBV00000000001861.pica |
035 | |a (DE-627)ELV049242695 | ||
035 | |a (ELSEVIER)S1096-7192(19)30979-5 | ||
040 | |a DE-627 |b ger |c DE-627 |e rakwb | ||
041 | |a eng | ||
082 | 0 | 4 | |a 610 |q VZ |
084 | |a 44.75 |2 bkl | ||
100 | 1 | |a Fumagalli, Francesca |e verfasserin |4 aut | |
245 | 1 | 0 | |a Lentiviral hematopoietic stem and progenitor cell gene therapy (HSPC-GT) for metachromatic leukodystrophy (MLD): Clinical outcomes from 33 patients |
264 | 1 | |c 2020 | |
336 | |a nicht spezifiziert |b zzz |2 rdacontent | ||
337 | |a nicht spezifiziert |b z |2 rdamedia | ||
338 | |a nicht spezifiziert |b zu |2 rdacarrier | ||
700 | 1 | |a Calbi, Valeria |4 oth | |
700 | 1 | |a Sessa, Maria |4 oth | |
700 | 1 | |a Zambon, Alberto |4 oth | |
700 | 1 | |a Baldoli, Cristina |4 oth | |
700 | 1 | |a Rancoita, Paula M.V. |4 oth | |
700 | 1 | |a Acquati, Serena |4 oth | |
700 | 1 | |a de Mattia, Fabiola |4 oth | |
700 | 1 | |a Tucci, Francesca |4 oth | |
700 | 1 | |a Gallo, Vera |4 oth | |
700 | 1 | |a Zancan, Stefano |4 oth | |
700 | 1 | |a Montini, Eugenio |4 oth | |
700 | 1 | |a Schwab, Laetitia |4 oth | |
700 | 1 | |a Downey, Gerald |4 oth | |
700 | 1 | |a Sharpe, John |4 oth | |
700 | 1 | |a Gabaldo, Michela |4 oth | |
700 | 1 | |a Martino, Sabata |4 oth | |
700 | 1 | |a De Serio, Clelia |4 oth | |
700 | 1 | |a Ciceri, Fabio |4 oth | |
700 | 1 | |a Filippi, Massimo |4 oth | |
700 | 1 | |a Sora, Maria Grazia Natali |4 oth | |
700 | 1 | |a Bernardo, Maria Ester |4 oth | |
700 | 1 | |a Naldini, Luigi |4 oth | |
700 | 1 | |a Biffi, Alessandra |4 oth | |
700 | 1 | |a Aiuti, Alessandro |4 oth | |
773 | 0 | 8 | |i Enthalten in |n Academic Press |a Worden, Lee ELSEVIER |t Measles transmission during a large outbreak in California |d 2019 |g Orlando, Fla |w (DE-627)ELV003843262 |
773 | 1 | 8 | |g volume:129 |g year:2020 |g number:2 |g pages:59 |
856 | 4 | 0 | |u https://doi.org/10.1016/j.ymgme.2019.11.135 |3 Volltext |
912 | |a GBV_USEFLAG_U | ||
912 | |a GBV_ELV | ||
912 | |a SYSFLAG_U | ||
912 | |a SSG-OLC-PHA | ||
936 | b | k | |a 44.75 |j Infektionskrankheiten |j parasitäre Krankheiten |x Medizin |q VZ |
951 | |a AR | ||
952 | |d 129 |j 2020 |e 2 |h 59 |y 129.2020, 2, S59- |
author_variant |
f f ff |
---|---|
matchkey_str |
fumagallifrancescacalbivaleriasessamaria:2020----:etvrleaooeiseadrgntreleehrphpgfreahoailuoytohm |
hierarchy_sort_str |
2020 |
bklnumber |
44.75 |
publishDate |
2020 |
allfields |
10.1016/j.ymgme.2019.11.135 doi /cbs_pica/cbs_olc/import_discovery/elsevier/einzuspielen/GBV00000000001861.pica (DE-627)ELV049242695 (ELSEVIER)S1096-7192(19)30979-5 DE-627 ger DE-627 rakwb eng 610 VZ 44.75 bkl Fumagalli, Francesca verfasserin aut Lentiviral hematopoietic stem and progenitor cell gene therapy (HSPC-GT) for metachromatic leukodystrophy (MLD): Clinical outcomes from 33 patients 2020 nicht spezifiziert zzz rdacontent nicht spezifiziert z rdamedia nicht spezifiziert zu rdacarrier Calbi, Valeria oth Sessa, Maria oth Zambon, Alberto oth Baldoli, Cristina oth Rancoita, Paula M.V. oth Acquati, Serena oth de Mattia, Fabiola oth Tucci, Francesca oth Gallo, Vera oth Zancan, Stefano oth Montini, Eugenio oth Schwab, Laetitia oth Downey, Gerald oth Sharpe, John oth Gabaldo, Michela oth Martino, Sabata oth De Serio, Clelia oth Ciceri, Fabio oth Filippi, Massimo oth Sora, Maria Grazia Natali oth Bernardo, Maria Ester oth Naldini, Luigi oth Biffi, Alessandra oth Aiuti, Alessandro oth Enthalten in Academic Press Worden, Lee ELSEVIER Measles transmission during a large outbreak in California 2019 Orlando, Fla (DE-627)ELV003843262 volume:129 year:2020 number:2 pages:59 https://doi.org/10.1016/j.ymgme.2019.11.135 Volltext GBV_USEFLAG_U GBV_ELV SYSFLAG_U SSG-OLC-PHA 44.75 Infektionskrankheiten parasitäre Krankheiten Medizin VZ AR 129 2020 2 59 129.2020, 2, S59- |
spelling |
10.1016/j.ymgme.2019.11.135 doi /cbs_pica/cbs_olc/import_discovery/elsevier/einzuspielen/GBV00000000001861.pica (DE-627)ELV049242695 (ELSEVIER)S1096-7192(19)30979-5 DE-627 ger DE-627 rakwb eng 610 VZ 44.75 bkl Fumagalli, Francesca verfasserin aut Lentiviral hematopoietic stem and progenitor cell gene therapy (HSPC-GT) for metachromatic leukodystrophy (MLD): Clinical outcomes from 33 patients 2020 nicht spezifiziert zzz rdacontent nicht spezifiziert z rdamedia nicht spezifiziert zu rdacarrier Calbi, Valeria oth Sessa, Maria oth Zambon, Alberto oth Baldoli, Cristina oth Rancoita, Paula M.V. oth Acquati, Serena oth de Mattia, Fabiola oth Tucci, Francesca oth Gallo, Vera oth Zancan, Stefano oth Montini, Eugenio oth Schwab, Laetitia oth Downey, Gerald oth Sharpe, John oth Gabaldo, Michela oth Martino, Sabata oth De Serio, Clelia oth Ciceri, Fabio oth Filippi, Massimo oth Sora, Maria Grazia Natali oth Bernardo, Maria Ester oth Naldini, Luigi oth Biffi, Alessandra oth Aiuti, Alessandro oth Enthalten in Academic Press Worden, Lee ELSEVIER Measles transmission during a large outbreak in California 2019 Orlando, Fla (DE-627)ELV003843262 volume:129 year:2020 number:2 pages:59 https://doi.org/10.1016/j.ymgme.2019.11.135 Volltext GBV_USEFLAG_U GBV_ELV SYSFLAG_U SSG-OLC-PHA 44.75 Infektionskrankheiten parasitäre Krankheiten Medizin VZ AR 129 2020 2 59 129.2020, 2, S59- |
allfields_unstemmed |
10.1016/j.ymgme.2019.11.135 doi /cbs_pica/cbs_olc/import_discovery/elsevier/einzuspielen/GBV00000000001861.pica (DE-627)ELV049242695 (ELSEVIER)S1096-7192(19)30979-5 DE-627 ger DE-627 rakwb eng 610 VZ 44.75 bkl Fumagalli, Francesca verfasserin aut Lentiviral hematopoietic stem and progenitor cell gene therapy (HSPC-GT) for metachromatic leukodystrophy (MLD): Clinical outcomes from 33 patients 2020 nicht spezifiziert zzz rdacontent nicht spezifiziert z rdamedia nicht spezifiziert zu rdacarrier Calbi, Valeria oth Sessa, Maria oth Zambon, Alberto oth Baldoli, Cristina oth Rancoita, Paula M.V. oth Acquati, Serena oth de Mattia, Fabiola oth Tucci, Francesca oth Gallo, Vera oth Zancan, Stefano oth Montini, Eugenio oth Schwab, Laetitia oth Downey, Gerald oth Sharpe, John oth Gabaldo, Michela oth Martino, Sabata oth De Serio, Clelia oth Ciceri, Fabio oth Filippi, Massimo oth Sora, Maria Grazia Natali oth Bernardo, Maria Ester oth Naldini, Luigi oth Biffi, Alessandra oth Aiuti, Alessandro oth Enthalten in Academic Press Worden, Lee ELSEVIER Measles transmission during a large outbreak in California 2019 Orlando, Fla (DE-627)ELV003843262 volume:129 year:2020 number:2 pages:59 https://doi.org/10.1016/j.ymgme.2019.11.135 Volltext GBV_USEFLAG_U GBV_ELV SYSFLAG_U SSG-OLC-PHA 44.75 Infektionskrankheiten parasitäre Krankheiten Medizin VZ AR 129 2020 2 59 129.2020, 2, S59- |
allfieldsGer |
10.1016/j.ymgme.2019.11.135 doi /cbs_pica/cbs_olc/import_discovery/elsevier/einzuspielen/GBV00000000001861.pica (DE-627)ELV049242695 (ELSEVIER)S1096-7192(19)30979-5 DE-627 ger DE-627 rakwb eng 610 VZ 44.75 bkl Fumagalli, Francesca verfasserin aut Lentiviral hematopoietic stem and progenitor cell gene therapy (HSPC-GT) for metachromatic leukodystrophy (MLD): Clinical outcomes from 33 patients 2020 nicht spezifiziert zzz rdacontent nicht spezifiziert z rdamedia nicht spezifiziert zu rdacarrier Calbi, Valeria oth Sessa, Maria oth Zambon, Alberto oth Baldoli, Cristina oth Rancoita, Paula M.V. oth Acquati, Serena oth de Mattia, Fabiola oth Tucci, Francesca oth Gallo, Vera oth Zancan, Stefano oth Montini, Eugenio oth Schwab, Laetitia oth Downey, Gerald oth Sharpe, John oth Gabaldo, Michela oth Martino, Sabata oth De Serio, Clelia oth Ciceri, Fabio oth Filippi, Massimo oth Sora, Maria Grazia Natali oth Bernardo, Maria Ester oth Naldini, Luigi oth Biffi, Alessandra oth Aiuti, Alessandro oth Enthalten in Academic Press Worden, Lee ELSEVIER Measles transmission during a large outbreak in California 2019 Orlando, Fla (DE-627)ELV003843262 volume:129 year:2020 number:2 pages:59 https://doi.org/10.1016/j.ymgme.2019.11.135 Volltext GBV_USEFLAG_U GBV_ELV SYSFLAG_U SSG-OLC-PHA 44.75 Infektionskrankheiten parasitäre Krankheiten Medizin VZ AR 129 2020 2 59 129.2020, 2, S59- |
allfieldsSound |
10.1016/j.ymgme.2019.11.135 doi /cbs_pica/cbs_olc/import_discovery/elsevier/einzuspielen/GBV00000000001861.pica (DE-627)ELV049242695 (ELSEVIER)S1096-7192(19)30979-5 DE-627 ger DE-627 rakwb eng 610 VZ 44.75 bkl Fumagalli, Francesca verfasserin aut Lentiviral hematopoietic stem and progenitor cell gene therapy (HSPC-GT) for metachromatic leukodystrophy (MLD): Clinical outcomes from 33 patients 2020 nicht spezifiziert zzz rdacontent nicht spezifiziert z rdamedia nicht spezifiziert zu rdacarrier Calbi, Valeria oth Sessa, Maria oth Zambon, Alberto oth Baldoli, Cristina oth Rancoita, Paula M.V. oth Acquati, Serena oth de Mattia, Fabiola oth Tucci, Francesca oth Gallo, Vera oth Zancan, Stefano oth Montini, Eugenio oth Schwab, Laetitia oth Downey, Gerald oth Sharpe, John oth Gabaldo, Michela oth Martino, Sabata oth De Serio, Clelia oth Ciceri, Fabio oth Filippi, Massimo oth Sora, Maria Grazia Natali oth Bernardo, Maria Ester oth Naldini, Luigi oth Biffi, Alessandra oth Aiuti, Alessandro oth Enthalten in Academic Press Worden, Lee ELSEVIER Measles transmission during a large outbreak in California 2019 Orlando, Fla (DE-627)ELV003843262 volume:129 year:2020 number:2 pages:59 https://doi.org/10.1016/j.ymgme.2019.11.135 Volltext GBV_USEFLAG_U GBV_ELV SYSFLAG_U SSG-OLC-PHA 44.75 Infektionskrankheiten parasitäre Krankheiten Medizin VZ AR 129 2020 2 59 129.2020, 2, S59- |
language |
English |
source |
Enthalten in Measles transmission during a large outbreak in California Orlando, Fla volume:129 year:2020 number:2 pages:59 |
sourceStr |
Enthalten in Measles transmission during a large outbreak in California Orlando, Fla volume:129 year:2020 number:2 pages:59 |
format_phy_str_mv |
Article |
bklname |
Infektionskrankheiten parasitäre Krankheiten |
institution |
findex.gbv.de |
dewey-raw |
610 |
isfreeaccess_bool |
false |
container_title |
Measles transmission during a large outbreak in California |
authorswithroles_txt_mv |
Fumagalli, Francesca @@aut@@ Calbi, Valeria @@oth@@ Sessa, Maria @@oth@@ Zambon, Alberto @@oth@@ Baldoli, Cristina @@oth@@ Rancoita, Paula M.V. @@oth@@ Acquati, Serena @@oth@@ de Mattia, Fabiola @@oth@@ Tucci, Francesca @@oth@@ Gallo, Vera @@oth@@ Zancan, Stefano @@oth@@ Montini, Eugenio @@oth@@ Schwab, Laetitia @@oth@@ Downey, Gerald @@oth@@ Sharpe, John @@oth@@ Gabaldo, Michela @@oth@@ Martino, Sabata @@oth@@ De Serio, Clelia @@oth@@ Ciceri, Fabio @@oth@@ Filippi, Massimo @@oth@@ Sora, Maria Grazia Natali @@oth@@ Bernardo, Maria Ester @@oth@@ Naldini, Luigi @@oth@@ Biffi, Alessandra @@oth@@ Aiuti, Alessandro @@oth@@ |
publishDateDaySort_date |
2020-01-01T00:00:00Z |
hierarchy_top_id |
ELV003843262 |
dewey-sort |
3610 |
id |
ELV049242695 |
language_de |
englisch |
fullrecord |
<?xml version="1.0" encoding="UTF-8"?><collection xmlns="http://www.loc.gov/MARC21/slim"><record><leader>01000caa a22002652 4500</leader><controlfield tag="001">ELV049242695</controlfield><controlfield tag="003">DE-627</controlfield><controlfield tag="005">20230624152937.0</controlfield><controlfield tag="007">cr uuu---uuuuu</controlfield><controlfield tag="008">200518s2020 xx |||||o 00| ||eng c</controlfield><datafield tag="024" ind1="7" ind2=" "><subfield code="a">10.1016/j.ymgme.2019.11.135</subfield><subfield code="2">doi</subfield></datafield><datafield tag="028" ind1="5" ind2="2"><subfield code="a">/cbs_pica/cbs_olc/import_discovery/elsevier/einzuspielen/GBV00000000001861.pica</subfield></datafield><datafield tag="035" ind1=" " ind2=" "><subfield code="a">(DE-627)ELV049242695</subfield></datafield><datafield tag="035" ind1=" " ind2=" "><subfield code="a">(ELSEVIER)S1096-7192(19)30979-5</subfield></datafield><datafield tag="040" ind1=" " ind2=" "><subfield code="a">DE-627</subfield><subfield code="b">ger</subfield><subfield code="c">DE-627</subfield><subfield code="e">rakwb</subfield></datafield><datafield tag="041" ind1=" " ind2=" "><subfield code="a">eng</subfield></datafield><datafield tag="082" ind1="0" ind2="4"><subfield code="a">610</subfield><subfield code="q">VZ</subfield></datafield><datafield tag="084" ind1=" " ind2=" "><subfield code="a">44.75</subfield><subfield code="2">bkl</subfield></datafield><datafield tag="100" ind1="1" ind2=" "><subfield code="a">Fumagalli, Francesca</subfield><subfield code="e">verfasserin</subfield><subfield code="4">aut</subfield></datafield><datafield tag="245" ind1="1" ind2="0"><subfield code="a">Lentiviral hematopoietic stem and progenitor cell gene therapy (HSPC-GT) for metachromatic leukodystrophy (MLD): Clinical outcomes from 33 patients</subfield></datafield><datafield tag="264" ind1=" " ind2="1"><subfield code="c">2020</subfield></datafield><datafield tag="336" ind1=" " ind2=" "><subfield code="a">nicht spezifiziert</subfield><subfield code="b">zzz</subfield><subfield code="2">rdacontent</subfield></datafield><datafield tag="337" ind1=" " ind2=" "><subfield code="a">nicht spezifiziert</subfield><subfield code="b">z</subfield><subfield code="2">rdamedia</subfield></datafield><datafield tag="338" ind1=" " ind2=" "><subfield code="a">nicht spezifiziert</subfield><subfield code="b">zu</subfield><subfield code="2">rdacarrier</subfield></datafield><datafield tag="700" ind1="1" ind2=" "><subfield code="a">Calbi, Valeria</subfield><subfield code="4">oth</subfield></datafield><datafield tag="700" ind1="1" ind2=" "><subfield code="a">Sessa, Maria</subfield><subfield code="4">oth</subfield></datafield><datafield tag="700" ind1="1" ind2=" "><subfield code="a">Zambon, Alberto</subfield><subfield code="4">oth</subfield></datafield><datafield tag="700" ind1="1" ind2=" "><subfield code="a">Baldoli, Cristina</subfield><subfield code="4">oth</subfield></datafield><datafield tag="700" ind1="1" ind2=" "><subfield code="a">Rancoita, Paula M.V.</subfield><subfield code="4">oth</subfield></datafield><datafield tag="700" ind1="1" ind2=" "><subfield code="a">Acquati, Serena</subfield><subfield code="4">oth</subfield></datafield><datafield tag="700" ind1="1" ind2=" "><subfield code="a">de Mattia, Fabiola</subfield><subfield code="4">oth</subfield></datafield><datafield tag="700" ind1="1" ind2=" "><subfield code="a">Tucci, Francesca</subfield><subfield code="4">oth</subfield></datafield><datafield tag="700" ind1="1" ind2=" "><subfield code="a">Gallo, Vera</subfield><subfield code="4">oth</subfield></datafield><datafield tag="700" ind1="1" ind2=" "><subfield code="a">Zancan, Stefano</subfield><subfield code="4">oth</subfield></datafield><datafield tag="700" ind1="1" ind2=" "><subfield code="a">Montini, Eugenio</subfield><subfield code="4">oth</subfield></datafield><datafield tag="700" ind1="1" ind2=" "><subfield code="a">Schwab, Laetitia</subfield><subfield code="4">oth</subfield></datafield><datafield tag="700" ind1="1" ind2=" "><subfield code="a">Downey, Gerald</subfield><subfield code="4">oth</subfield></datafield><datafield tag="700" ind1="1" ind2=" "><subfield code="a">Sharpe, John</subfield><subfield code="4">oth</subfield></datafield><datafield tag="700" ind1="1" ind2=" "><subfield code="a">Gabaldo, Michela</subfield><subfield code="4">oth</subfield></datafield><datafield tag="700" ind1="1" ind2=" "><subfield code="a">Martino, Sabata</subfield><subfield code="4">oth</subfield></datafield><datafield tag="700" ind1="1" ind2=" "><subfield code="a">De Serio, Clelia</subfield><subfield code="4">oth</subfield></datafield><datafield tag="700" ind1="1" ind2=" "><subfield code="a">Ciceri, Fabio</subfield><subfield code="4">oth</subfield></datafield><datafield tag="700" ind1="1" ind2=" "><subfield code="a">Filippi, Massimo</subfield><subfield code="4">oth</subfield></datafield><datafield tag="700" ind1="1" ind2=" "><subfield code="a">Sora, Maria Grazia Natali</subfield><subfield code="4">oth</subfield></datafield><datafield tag="700" ind1="1" ind2=" "><subfield code="a">Bernardo, Maria Ester</subfield><subfield code="4">oth</subfield></datafield><datafield tag="700" ind1="1" ind2=" "><subfield code="a">Naldini, Luigi</subfield><subfield code="4">oth</subfield></datafield><datafield tag="700" ind1="1" ind2=" "><subfield code="a">Biffi, Alessandra</subfield><subfield code="4">oth</subfield></datafield><datafield tag="700" ind1="1" ind2=" "><subfield code="a">Aiuti, Alessandro</subfield><subfield code="4">oth</subfield></datafield><datafield tag="773" ind1="0" ind2="8"><subfield code="i">Enthalten in</subfield><subfield code="n">Academic Press</subfield><subfield code="a">Worden, Lee ELSEVIER</subfield><subfield code="t">Measles transmission during a large outbreak in California</subfield><subfield code="d">2019</subfield><subfield code="g">Orlando, Fla</subfield><subfield code="w">(DE-627)ELV003843262</subfield></datafield><datafield tag="773" ind1="1" ind2="8"><subfield code="g">volume:129</subfield><subfield code="g">year:2020</subfield><subfield code="g">number:2</subfield><subfield code="g">pages:59</subfield></datafield><datafield tag="856" ind1="4" ind2="0"><subfield code="u">https://doi.org/10.1016/j.ymgme.2019.11.135</subfield><subfield code="3">Volltext</subfield></datafield><datafield tag="912" ind1=" " ind2=" "><subfield code="a">GBV_USEFLAG_U</subfield></datafield><datafield tag="912" ind1=" " ind2=" "><subfield code="a">GBV_ELV</subfield></datafield><datafield tag="912" ind1=" " ind2=" "><subfield code="a">SYSFLAG_U</subfield></datafield><datafield tag="912" ind1=" " ind2=" "><subfield code="a">SSG-OLC-PHA</subfield></datafield><datafield tag="936" ind1="b" ind2="k"><subfield code="a">44.75</subfield><subfield code="j">Infektionskrankheiten</subfield><subfield code="j">parasitäre Krankheiten</subfield><subfield code="x">Medizin</subfield><subfield code="q">VZ</subfield></datafield><datafield tag="951" ind1=" " ind2=" "><subfield code="a">AR</subfield></datafield><datafield tag="952" ind1=" " ind2=" "><subfield code="d">129</subfield><subfield code="j">2020</subfield><subfield code="e">2</subfield><subfield code="h">59</subfield><subfield code="y">129.2020, 2, S59-</subfield></datafield></record></collection>
|
author |
Fumagalli, Francesca |
spellingShingle |
Fumagalli, Francesca ddc 610 bkl 44.75 Lentiviral hematopoietic stem and progenitor cell gene therapy (HSPC-GT) for metachromatic leukodystrophy (MLD): Clinical outcomes from 33 patients |
authorStr |
Fumagalli, Francesca |
ppnlink_with_tag_str_mv |
@@773@@(DE-627)ELV003843262 |
format |
electronic Article |
dewey-ones |
610 - Medicine & health |
delete_txt_mv |
keep |
author_role |
aut |
collection |
elsevier |
remote_str |
true |
illustrated |
Not Illustrated |
topic_title |
610 VZ 44.75 bkl Lentiviral hematopoietic stem and progenitor cell gene therapy (HSPC-GT) for metachromatic leukodystrophy (MLD): Clinical outcomes from 33 patients |
topic |
ddc 610 bkl 44.75 |
topic_unstemmed |
ddc 610 bkl 44.75 |
topic_browse |
ddc 610 bkl 44.75 |
format_facet |
Elektronische Aufsätze Aufsätze Elektronische Ressource |
format_main_str_mv |
Text Zeitschrift/Artikel |
carriertype_str_mv |
zu |
author2_variant |
v c vc m s ms a z az c b cb p m r pm pmr s a sa m f d mf mfd f t ft v g vg s z sz e m em l s ls g d gd j s js m g mg s m sm s c d sc scd f c fc m f mf m g n s mgn mgns m e b me meb l n ln a b ab a a aa |
hierarchy_parent_title |
Measles transmission during a large outbreak in California |
hierarchy_parent_id |
ELV003843262 |
dewey-tens |
610 - Medicine & health |
hierarchy_top_title |
Measles transmission during a large outbreak in California |
isfreeaccess_txt |
false |
familylinks_str_mv |
(DE-627)ELV003843262 |
title |
Lentiviral hematopoietic stem and progenitor cell gene therapy (HSPC-GT) for metachromatic leukodystrophy (MLD): Clinical outcomes from 33 patients |
ctrlnum |
(DE-627)ELV049242695 (ELSEVIER)S1096-7192(19)30979-5 |
title_full |
Lentiviral hematopoietic stem and progenitor cell gene therapy (HSPC-GT) for metachromatic leukodystrophy (MLD): Clinical outcomes from 33 patients |
author_sort |
Fumagalli, Francesca |
journal |
Measles transmission during a large outbreak in California |
journalStr |
Measles transmission during a large outbreak in California |
lang_code |
eng |
isOA_bool |
false |
dewey-hundreds |
600 - Technology |
recordtype |
marc |
publishDateSort |
2020 |
contenttype_str_mv |
zzz |
container_start_page |
59 |
author_browse |
Fumagalli, Francesca |
container_volume |
129 |
class |
610 VZ 44.75 bkl |
format_se |
Elektronische Aufsätze |
author-letter |
Fumagalli, Francesca |
doi_str_mv |
10.1016/j.ymgme.2019.11.135 |
dewey-full |
610 |
title_sort |
lentiviral hematopoietic stem and progenitor cell gene therapy (hspc-gt) for metachromatic leukodystrophy (mld): clinical outcomes from 33 patients |
title_auth |
Lentiviral hematopoietic stem and progenitor cell gene therapy (HSPC-GT) for metachromatic leukodystrophy (MLD): Clinical outcomes from 33 patients |
collection_details |
GBV_USEFLAG_U GBV_ELV SYSFLAG_U SSG-OLC-PHA |
container_issue |
2 |
title_short |
Lentiviral hematopoietic stem and progenitor cell gene therapy (HSPC-GT) for metachromatic leukodystrophy (MLD): Clinical outcomes from 33 patients |
url |
https://doi.org/10.1016/j.ymgme.2019.11.135 |
remote_bool |
true |
author2 |
Calbi, Valeria Sessa, Maria Zambon, Alberto Baldoli, Cristina Rancoita, Paula M.V. Acquati, Serena de Mattia, Fabiola Tucci, Francesca Gallo, Vera Zancan, Stefano Montini, Eugenio Schwab, Laetitia Downey, Gerald Sharpe, John Gabaldo, Michela Martino, Sabata De Serio, Clelia Ciceri, Fabio Filippi, Massimo Sora, Maria Grazia Natali Bernardo, Maria Ester Naldini, Luigi Biffi, Alessandra Aiuti, Alessandro |
author2Str |
Calbi, Valeria Sessa, Maria Zambon, Alberto Baldoli, Cristina Rancoita, Paula M.V. Acquati, Serena de Mattia, Fabiola Tucci, Francesca Gallo, Vera Zancan, Stefano Montini, Eugenio Schwab, Laetitia Downey, Gerald Sharpe, John Gabaldo, Michela Martino, Sabata De Serio, Clelia Ciceri, Fabio Filippi, Massimo Sora, Maria Grazia Natali Bernardo, Maria Ester Naldini, Luigi Biffi, Alessandra Aiuti, Alessandro |
ppnlink |
ELV003843262 |
mediatype_str_mv |
z |
isOA_txt |
false |
hochschulschrift_bool |
false |
author2_role |
oth oth oth oth oth oth oth oth oth oth oth oth oth oth oth oth oth oth oth oth oth oth oth oth |
doi_str |
10.1016/j.ymgme.2019.11.135 |
up_date |
2024-07-06T21:01:47.573Z |
_version_ |
1803864986169114624 |
fullrecord_marcxml |
<?xml version="1.0" encoding="UTF-8"?><collection xmlns="http://www.loc.gov/MARC21/slim"><record><leader>01000caa a22002652 4500</leader><controlfield tag="001">ELV049242695</controlfield><controlfield tag="003">DE-627</controlfield><controlfield tag="005">20230624152937.0</controlfield><controlfield tag="007">cr uuu---uuuuu</controlfield><controlfield tag="008">200518s2020 xx |||||o 00| ||eng c</controlfield><datafield tag="024" ind1="7" ind2=" "><subfield code="a">10.1016/j.ymgme.2019.11.135</subfield><subfield code="2">doi</subfield></datafield><datafield tag="028" ind1="5" ind2="2"><subfield code="a">/cbs_pica/cbs_olc/import_discovery/elsevier/einzuspielen/GBV00000000001861.pica</subfield></datafield><datafield tag="035" ind1=" " ind2=" "><subfield code="a">(DE-627)ELV049242695</subfield></datafield><datafield tag="035" ind1=" " ind2=" "><subfield code="a">(ELSEVIER)S1096-7192(19)30979-5</subfield></datafield><datafield tag="040" ind1=" " ind2=" "><subfield code="a">DE-627</subfield><subfield code="b">ger</subfield><subfield code="c">DE-627</subfield><subfield code="e">rakwb</subfield></datafield><datafield tag="041" ind1=" " ind2=" "><subfield code="a">eng</subfield></datafield><datafield tag="082" ind1="0" ind2="4"><subfield code="a">610</subfield><subfield code="q">VZ</subfield></datafield><datafield tag="084" ind1=" " ind2=" "><subfield code="a">44.75</subfield><subfield code="2">bkl</subfield></datafield><datafield tag="100" ind1="1" ind2=" "><subfield code="a">Fumagalli, Francesca</subfield><subfield code="e">verfasserin</subfield><subfield code="4">aut</subfield></datafield><datafield tag="245" ind1="1" ind2="0"><subfield code="a">Lentiviral hematopoietic stem and progenitor cell gene therapy (HSPC-GT) for metachromatic leukodystrophy (MLD): Clinical outcomes from 33 patients</subfield></datafield><datafield tag="264" ind1=" " ind2="1"><subfield code="c">2020</subfield></datafield><datafield tag="336" ind1=" " ind2=" "><subfield code="a">nicht spezifiziert</subfield><subfield code="b">zzz</subfield><subfield code="2">rdacontent</subfield></datafield><datafield tag="337" ind1=" " ind2=" "><subfield code="a">nicht spezifiziert</subfield><subfield code="b">z</subfield><subfield code="2">rdamedia</subfield></datafield><datafield tag="338" ind1=" " ind2=" "><subfield code="a">nicht spezifiziert</subfield><subfield code="b">zu</subfield><subfield code="2">rdacarrier</subfield></datafield><datafield tag="700" ind1="1" ind2=" "><subfield code="a">Calbi, Valeria</subfield><subfield code="4">oth</subfield></datafield><datafield tag="700" ind1="1" ind2=" "><subfield code="a">Sessa, Maria</subfield><subfield code="4">oth</subfield></datafield><datafield tag="700" ind1="1" ind2=" "><subfield code="a">Zambon, Alberto</subfield><subfield code="4">oth</subfield></datafield><datafield tag="700" ind1="1" ind2=" "><subfield code="a">Baldoli, Cristina</subfield><subfield code="4">oth</subfield></datafield><datafield tag="700" ind1="1" ind2=" "><subfield code="a">Rancoita, Paula M.V.</subfield><subfield code="4">oth</subfield></datafield><datafield tag="700" ind1="1" ind2=" "><subfield code="a">Acquati, Serena</subfield><subfield code="4">oth</subfield></datafield><datafield tag="700" ind1="1" ind2=" "><subfield code="a">de Mattia, Fabiola</subfield><subfield code="4">oth</subfield></datafield><datafield tag="700" ind1="1" ind2=" "><subfield code="a">Tucci, Francesca</subfield><subfield code="4">oth</subfield></datafield><datafield tag="700" ind1="1" ind2=" "><subfield code="a">Gallo, Vera</subfield><subfield code="4">oth</subfield></datafield><datafield tag="700" ind1="1" ind2=" "><subfield code="a">Zancan, Stefano</subfield><subfield code="4">oth</subfield></datafield><datafield tag="700" ind1="1" ind2=" "><subfield code="a">Montini, Eugenio</subfield><subfield code="4">oth</subfield></datafield><datafield tag="700" ind1="1" ind2=" "><subfield code="a">Schwab, Laetitia</subfield><subfield code="4">oth</subfield></datafield><datafield tag="700" ind1="1" ind2=" "><subfield code="a">Downey, Gerald</subfield><subfield code="4">oth</subfield></datafield><datafield tag="700" ind1="1" ind2=" "><subfield code="a">Sharpe, John</subfield><subfield code="4">oth</subfield></datafield><datafield tag="700" ind1="1" ind2=" "><subfield code="a">Gabaldo, Michela</subfield><subfield code="4">oth</subfield></datafield><datafield tag="700" ind1="1" ind2=" "><subfield code="a">Martino, Sabata</subfield><subfield code="4">oth</subfield></datafield><datafield tag="700" ind1="1" ind2=" "><subfield code="a">De Serio, Clelia</subfield><subfield code="4">oth</subfield></datafield><datafield tag="700" ind1="1" ind2=" "><subfield code="a">Ciceri, Fabio</subfield><subfield code="4">oth</subfield></datafield><datafield tag="700" ind1="1" ind2=" "><subfield code="a">Filippi, Massimo</subfield><subfield code="4">oth</subfield></datafield><datafield tag="700" ind1="1" ind2=" "><subfield code="a">Sora, Maria Grazia Natali</subfield><subfield code="4">oth</subfield></datafield><datafield tag="700" ind1="1" ind2=" "><subfield code="a">Bernardo, Maria Ester</subfield><subfield code="4">oth</subfield></datafield><datafield tag="700" ind1="1" ind2=" "><subfield code="a">Naldini, Luigi</subfield><subfield code="4">oth</subfield></datafield><datafield tag="700" ind1="1" ind2=" "><subfield code="a">Biffi, Alessandra</subfield><subfield code="4">oth</subfield></datafield><datafield tag="700" ind1="1" ind2=" "><subfield code="a">Aiuti, Alessandro</subfield><subfield code="4">oth</subfield></datafield><datafield tag="773" ind1="0" ind2="8"><subfield code="i">Enthalten in</subfield><subfield code="n">Academic Press</subfield><subfield code="a">Worden, Lee ELSEVIER</subfield><subfield code="t">Measles transmission during a large outbreak in California</subfield><subfield code="d">2019</subfield><subfield code="g">Orlando, Fla</subfield><subfield code="w">(DE-627)ELV003843262</subfield></datafield><datafield tag="773" ind1="1" ind2="8"><subfield code="g">volume:129</subfield><subfield code="g">year:2020</subfield><subfield code="g">number:2</subfield><subfield code="g">pages:59</subfield></datafield><datafield tag="856" ind1="4" ind2="0"><subfield code="u">https://doi.org/10.1016/j.ymgme.2019.11.135</subfield><subfield code="3">Volltext</subfield></datafield><datafield tag="912" ind1=" " ind2=" "><subfield code="a">GBV_USEFLAG_U</subfield></datafield><datafield tag="912" ind1=" " ind2=" "><subfield code="a">GBV_ELV</subfield></datafield><datafield tag="912" ind1=" " ind2=" "><subfield code="a">SYSFLAG_U</subfield></datafield><datafield tag="912" ind1=" " ind2=" "><subfield code="a">SSG-OLC-PHA</subfield></datafield><datafield tag="936" ind1="b" ind2="k"><subfield code="a">44.75</subfield><subfield code="j">Infektionskrankheiten</subfield><subfield code="j">parasitäre Krankheiten</subfield><subfield code="x">Medizin</subfield><subfield code="q">VZ</subfield></datafield><datafield tag="951" ind1=" " ind2=" "><subfield code="a">AR</subfield></datafield><datafield tag="952" ind1=" " ind2=" "><subfield code="d">129</subfield><subfield code="j">2020</subfield><subfield code="e">2</subfield><subfield code="h">59</subfield><subfield code="y">129.2020, 2, S59-</subfield></datafield></record></collection>
|
score |
7.4005365 |