Lentiviral haematopoietic stem cell gene therapy for metachromatic leukodystrophy: Results in nine patients treated with a cryopreserved formulation of OTL-200
Autor*in: |
Calbi, Valeria [verfasserIn] |
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Format: |
E-Artikel |
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Sprache: |
Englisch |
Erschienen: |
2021 |
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Umfang: |
2 |
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Übergeordnetes Werk: |
Enthalten in: Measles transmission during a large outbreak in California - Worden, Lee ELSEVIER, 2019, Orlando, Fla |
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Übergeordnetes Werk: |
volume:132 ; year:2021 ; number:2 ; pages:21-22 ; extent:2 |
Links: |
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DOI / URN: |
10.1016/j.ymgme.2020.12.031 |
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lentiviral haematopoietic stem cell gene therapy for metachromatic leukodystrophy: results in nine patients treated with a cryopreserved formulation of otl-200 |
title_auth |
Lentiviral haematopoietic stem cell gene therapy for metachromatic leukodystrophy: Results in nine patients treated with a cryopreserved formulation of OTL-200 |
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title_short |
Lentiviral haematopoietic stem cell gene therapy for metachromatic leukodystrophy: Results in nine patients treated with a cryopreserved formulation of OTL-200 |
url |
https://doi.org/10.1016/j.ymgme.2020.12.031 |
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author2 |
Fumagalli, Francesca De Mattia, Fabiola Fratini, Elena Ferrua, Francesca Barzaghi, Federica Cicalese, Maria Pia Migliavacca, Maddalena Tucci, Francesca Gallo, Vera Ciotti, Francesca Fraschini, Maddalena Sarzana, Marina Locatelli, Sara Sangalli, Mara Morena, Francesco Segovia, Jesus Schwab, Laetitia C. Downey, Gerald Martino, Sabata Ciceri, Fabio Bernardo, Maria Ester Naldini, Luigi Aiuti, Alessandro |
author2Str |
Fumagalli, Francesca De Mattia, Fabiola Fratini, Elena Ferrua, Francesca Barzaghi, Federica Cicalese, Maria Pia Migliavacca, Maddalena Tucci, Francesca Gallo, Vera Ciotti, Francesca Fraschini, Maddalena Sarzana, Marina Locatelli, Sara Sangalli, Mara Morena, Francesco Segovia, Jesus Schwab, Laetitia C. Downey, Gerald Martino, Sabata Ciceri, Fabio Bernardo, Maria Ester Naldini, Luigi Aiuti, Alessandro |
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doi_str |
10.1016/j.ymgme.2020.12.031 |
up_date |
2024-07-06T17:34:38.229Z |
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