Lentiviral hematopoietic stem cell gene therapy (atidarsagene autotemcel) for late juvenile metachromatic leukodystrophy (MLD)
Autor*in: |
Gallo, Vera [verfasserIn] Calbi, Valeria [verfasserIn] De Mattia, Fabiola [verfasserIn] Zambon, Alberto Andrea [verfasserIn] Recupero, Salvatore [verfasserIn] Fratini, Elena Sophia [verfasserIn] Ciotti, Francesca [verfasserIn] Fraschini, Maddalena [verfasserIn] Sangalli, Mara [verfasserIn] Sarzana, Marina [verfasserIn] Clerici, Alessandra [verfasserIn] Morena, Francesco [verfasserIn] Martino, Sabata [verfasserIn] Brooks, Jean [verfasserIn] Richardson, Alan [verfasserIn] Campbell, Laura [verfasserIn] Aiuti, Alessandro [verfasserIn] Fumagalli, Francesca [verfasserIn] |
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Format: |
E-Artikel |
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Sprache: |
Englisch |
Erschienen: |
2023 |
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Übergeordnetes Werk: |
Enthalten in: Molecular genetics and metabolism - Orlando, Fla. : Academic Press, 1998, 141 |
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Übergeordnetes Werk: |
volume:141 |
DOI / URN: |
10.1016/j.ymgme.2023.107835 |
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Katalog-ID: |
ELV066819334 |
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700 | 1 | |a De Mattia, Fabiola |e verfasserin |4 aut | |
700 | 1 | |a Zambon, Alberto Andrea |e verfasserin |4 aut | |
700 | 1 | |a Recupero, Salvatore |e verfasserin |4 aut | |
700 | 1 | |a Fratini, Elena Sophia |e verfasserin |4 aut | |
700 | 1 | |a Ciotti, Francesca |e verfasserin |4 aut | |
700 | 1 | |a Fraschini, Maddalena |e verfasserin |4 aut | |
700 | 1 | |a Sangalli, Mara |e verfasserin |4 aut | |
700 | 1 | |a Sarzana, Marina |e verfasserin |4 aut | |
700 | 1 | |a Clerici, Alessandra |e verfasserin |4 aut | |
700 | 1 | |a Morena, Francesco |e verfasserin |4 aut | |
700 | 1 | |a Martino, Sabata |e verfasserin |4 aut | |
700 | 1 | |a Brooks, Jean |e verfasserin |4 aut | |
700 | 1 | |a Richardson, Alan |e verfasserin |4 aut | |
700 | 1 | |a Campbell, Laura |e verfasserin |4 aut | |
700 | 1 | |a Aiuti, Alessandro |e verfasserin |4 aut | |
700 | 1 | |a Fumagalli, Francesca |e verfasserin |4 aut | |
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912 | |a GBV_ILN_4338 | ||
912 | |a GBV_ILN_4393 | ||
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2023 |
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2023 |
allfields |
10.1016/j.ymgme.2023.107835 doi (DE-627)ELV066819334 (ELSEVIER)S1096-7192(23)00465-1 DE-627 ger DE-627 rda eng 610 VZ 42.13 bkl 44.33 bkl Gallo, Vera verfasserin aut Lentiviral hematopoietic stem cell gene therapy (atidarsagene autotemcel) for late juvenile metachromatic leukodystrophy (MLD) 2023 nicht spezifiziert zzz rdacontent Computermedien c rdamedia Online-Ressource cr rdacarrier Calbi, Valeria verfasserin aut De Mattia, Fabiola verfasserin aut Zambon, Alberto Andrea verfasserin aut Recupero, Salvatore verfasserin aut Fratini, Elena Sophia verfasserin aut Ciotti, Francesca verfasserin aut Fraschini, Maddalena verfasserin aut Sangalli, Mara verfasserin aut Sarzana, Marina verfasserin aut Clerici, Alessandra verfasserin aut Morena, Francesco verfasserin aut Martino, Sabata verfasserin aut Brooks, Jean verfasserin aut Richardson, Alan verfasserin aut Campbell, Laura verfasserin aut Aiuti, Alessandro verfasserin aut Fumagalli, Francesca verfasserin aut Enthalten in Molecular genetics and metabolism Orlando, Fla. : Academic Press, 1998 141 Online-Ressource (DE-627)268125260 (DE-600)1471393-7 (DE-576)106869493 1096-7206 nnns volume:141 GBV_USEFLAG_U GBV_ELV SYSFLAG_U SSG-OLC-PHA GBV_ILN_20 GBV_ILN_22 GBV_ILN_23 GBV_ILN_24 GBV_ILN_31 GBV_ILN_32 GBV_ILN_40 GBV_ILN_60 GBV_ILN_62 GBV_ILN_65 GBV_ILN_69 GBV_ILN_70 GBV_ILN_73 GBV_ILN_74 GBV_ILN_90 GBV_ILN_100 GBV_ILN_101 GBV_ILN_105 GBV_ILN_110 GBV_ILN_151 GBV_ILN_187 GBV_ILN_213 GBV_ILN_224 GBV_ILN_230 GBV_ILN_370 GBV_ILN_602 GBV_ILN_702 GBV_ILN_2001 GBV_ILN_2003 GBV_ILN_2004 GBV_ILN_2005 GBV_ILN_2007 GBV_ILN_2008 GBV_ILN_2009 GBV_ILN_2010 GBV_ILN_2011 GBV_ILN_2014 GBV_ILN_2015 GBV_ILN_2020 GBV_ILN_2021 GBV_ILN_2025 GBV_ILN_2026 GBV_ILN_2027 GBV_ILN_2034 GBV_ILN_2044 GBV_ILN_2048 GBV_ILN_2049 GBV_ILN_2050 GBV_ILN_2055 GBV_ILN_2056 GBV_ILN_2059 GBV_ILN_2061 GBV_ILN_2064 GBV_ILN_2088 GBV_ILN_2106 GBV_ILN_2110 GBV_ILN_2111 GBV_ILN_2112 GBV_ILN_2122 GBV_ILN_2129 GBV_ILN_2143 GBV_ILN_2152 GBV_ILN_2153 GBV_ILN_2190 GBV_ILN_2232 GBV_ILN_2336 GBV_ILN_2470 GBV_ILN_2507 GBV_ILN_4035 GBV_ILN_4037 GBV_ILN_4112 GBV_ILN_4125 GBV_ILN_4242 GBV_ILN_4249 GBV_ILN_4251 GBV_ILN_4305 GBV_ILN_4306 GBV_ILN_4307 GBV_ILN_4313 GBV_ILN_4322 GBV_ILN_4323 GBV_ILN_4324 GBV_ILN_4325 GBV_ILN_4326 GBV_ILN_4333 GBV_ILN_4334 GBV_ILN_4338 GBV_ILN_4393 GBV_ILN_4700 42.13 Molekularbiologie VZ 44.33 Physiologische Chemie VZ AR 141 |
spelling |
10.1016/j.ymgme.2023.107835 doi (DE-627)ELV066819334 (ELSEVIER)S1096-7192(23)00465-1 DE-627 ger DE-627 rda eng 610 VZ 42.13 bkl 44.33 bkl Gallo, Vera verfasserin aut Lentiviral hematopoietic stem cell gene therapy (atidarsagene autotemcel) for late juvenile metachromatic leukodystrophy (MLD) 2023 nicht spezifiziert zzz rdacontent Computermedien c rdamedia Online-Ressource cr rdacarrier Calbi, Valeria verfasserin aut De Mattia, Fabiola verfasserin aut Zambon, Alberto Andrea verfasserin aut Recupero, Salvatore verfasserin aut Fratini, Elena Sophia verfasserin aut Ciotti, Francesca verfasserin aut Fraschini, Maddalena verfasserin aut Sangalli, Mara verfasserin aut Sarzana, Marina verfasserin aut Clerici, Alessandra verfasserin aut Morena, Francesco verfasserin aut Martino, Sabata verfasserin aut Brooks, Jean verfasserin aut Richardson, Alan verfasserin aut Campbell, Laura verfasserin aut Aiuti, Alessandro verfasserin aut Fumagalli, Francesca verfasserin aut Enthalten in Molecular genetics and metabolism Orlando, Fla. : Academic Press, 1998 141 Online-Ressource (DE-627)268125260 (DE-600)1471393-7 (DE-576)106869493 1096-7206 nnns volume:141 GBV_USEFLAG_U GBV_ELV SYSFLAG_U SSG-OLC-PHA GBV_ILN_20 GBV_ILN_22 GBV_ILN_23 GBV_ILN_24 GBV_ILN_31 GBV_ILN_32 GBV_ILN_40 GBV_ILN_60 GBV_ILN_62 GBV_ILN_65 GBV_ILN_69 GBV_ILN_70 GBV_ILN_73 GBV_ILN_74 GBV_ILN_90 GBV_ILN_100 GBV_ILN_101 GBV_ILN_105 GBV_ILN_110 GBV_ILN_151 GBV_ILN_187 GBV_ILN_213 GBV_ILN_224 GBV_ILN_230 GBV_ILN_370 GBV_ILN_602 GBV_ILN_702 GBV_ILN_2001 GBV_ILN_2003 GBV_ILN_2004 GBV_ILN_2005 GBV_ILN_2007 GBV_ILN_2008 GBV_ILN_2009 GBV_ILN_2010 GBV_ILN_2011 GBV_ILN_2014 GBV_ILN_2015 GBV_ILN_2020 GBV_ILN_2021 GBV_ILN_2025 GBV_ILN_2026 GBV_ILN_2027 GBV_ILN_2034 GBV_ILN_2044 GBV_ILN_2048 GBV_ILN_2049 GBV_ILN_2050 GBV_ILN_2055 GBV_ILN_2056 GBV_ILN_2059 GBV_ILN_2061 GBV_ILN_2064 GBV_ILN_2088 GBV_ILN_2106 GBV_ILN_2110 GBV_ILN_2111 GBV_ILN_2112 GBV_ILN_2122 GBV_ILN_2129 GBV_ILN_2143 GBV_ILN_2152 GBV_ILN_2153 GBV_ILN_2190 GBV_ILN_2232 GBV_ILN_2336 GBV_ILN_2470 GBV_ILN_2507 GBV_ILN_4035 GBV_ILN_4037 GBV_ILN_4112 GBV_ILN_4125 GBV_ILN_4242 GBV_ILN_4249 GBV_ILN_4251 GBV_ILN_4305 GBV_ILN_4306 GBV_ILN_4307 GBV_ILN_4313 GBV_ILN_4322 GBV_ILN_4323 GBV_ILN_4324 GBV_ILN_4325 GBV_ILN_4326 GBV_ILN_4333 GBV_ILN_4334 GBV_ILN_4338 GBV_ILN_4393 GBV_ILN_4700 42.13 Molekularbiologie VZ 44.33 Physiologische Chemie VZ AR 141 |
allfields_unstemmed |
10.1016/j.ymgme.2023.107835 doi (DE-627)ELV066819334 (ELSEVIER)S1096-7192(23)00465-1 DE-627 ger DE-627 rda eng 610 VZ 42.13 bkl 44.33 bkl Gallo, Vera verfasserin aut Lentiviral hematopoietic stem cell gene therapy (atidarsagene autotemcel) for late juvenile metachromatic leukodystrophy (MLD) 2023 nicht spezifiziert zzz rdacontent Computermedien c rdamedia Online-Ressource cr rdacarrier Calbi, Valeria verfasserin aut De Mattia, Fabiola verfasserin aut Zambon, Alberto Andrea verfasserin aut Recupero, Salvatore verfasserin aut Fratini, Elena Sophia verfasserin aut Ciotti, Francesca verfasserin aut Fraschini, Maddalena verfasserin aut Sangalli, Mara verfasserin aut Sarzana, Marina verfasserin aut Clerici, Alessandra verfasserin aut Morena, Francesco verfasserin aut Martino, Sabata verfasserin aut Brooks, Jean verfasserin aut Richardson, Alan verfasserin aut Campbell, Laura verfasserin aut Aiuti, Alessandro verfasserin aut Fumagalli, Francesca verfasserin aut Enthalten in Molecular genetics and metabolism Orlando, Fla. : Academic Press, 1998 141 Online-Ressource (DE-627)268125260 (DE-600)1471393-7 (DE-576)106869493 1096-7206 nnns volume:141 GBV_USEFLAG_U GBV_ELV SYSFLAG_U SSG-OLC-PHA GBV_ILN_20 GBV_ILN_22 GBV_ILN_23 GBV_ILN_24 GBV_ILN_31 GBV_ILN_32 GBV_ILN_40 GBV_ILN_60 GBV_ILN_62 GBV_ILN_65 GBV_ILN_69 GBV_ILN_70 GBV_ILN_73 GBV_ILN_74 GBV_ILN_90 GBV_ILN_100 GBV_ILN_101 GBV_ILN_105 GBV_ILN_110 GBV_ILN_151 GBV_ILN_187 GBV_ILN_213 GBV_ILN_224 GBV_ILN_230 GBV_ILN_370 GBV_ILN_602 GBV_ILN_702 GBV_ILN_2001 GBV_ILN_2003 GBV_ILN_2004 GBV_ILN_2005 GBV_ILN_2007 GBV_ILN_2008 GBV_ILN_2009 GBV_ILN_2010 GBV_ILN_2011 GBV_ILN_2014 GBV_ILN_2015 GBV_ILN_2020 GBV_ILN_2021 GBV_ILN_2025 GBV_ILN_2026 GBV_ILN_2027 GBV_ILN_2034 GBV_ILN_2044 GBV_ILN_2048 GBV_ILN_2049 GBV_ILN_2050 GBV_ILN_2055 GBV_ILN_2056 GBV_ILN_2059 GBV_ILN_2061 GBV_ILN_2064 GBV_ILN_2088 GBV_ILN_2106 GBV_ILN_2110 GBV_ILN_2111 GBV_ILN_2112 GBV_ILN_2122 GBV_ILN_2129 GBV_ILN_2143 GBV_ILN_2152 GBV_ILN_2153 GBV_ILN_2190 GBV_ILN_2232 GBV_ILN_2336 GBV_ILN_2470 GBV_ILN_2507 GBV_ILN_4035 GBV_ILN_4037 GBV_ILN_4112 GBV_ILN_4125 GBV_ILN_4242 GBV_ILN_4249 GBV_ILN_4251 GBV_ILN_4305 GBV_ILN_4306 GBV_ILN_4307 GBV_ILN_4313 GBV_ILN_4322 GBV_ILN_4323 GBV_ILN_4324 GBV_ILN_4325 GBV_ILN_4326 GBV_ILN_4333 GBV_ILN_4334 GBV_ILN_4338 GBV_ILN_4393 GBV_ILN_4700 42.13 Molekularbiologie VZ 44.33 Physiologische Chemie VZ AR 141 |
allfieldsGer |
10.1016/j.ymgme.2023.107835 doi (DE-627)ELV066819334 (ELSEVIER)S1096-7192(23)00465-1 DE-627 ger DE-627 rda eng 610 VZ 42.13 bkl 44.33 bkl Gallo, Vera verfasserin aut Lentiviral hematopoietic stem cell gene therapy (atidarsagene autotemcel) for late juvenile metachromatic leukodystrophy (MLD) 2023 nicht spezifiziert zzz rdacontent Computermedien c rdamedia Online-Ressource cr rdacarrier Calbi, Valeria verfasserin aut De Mattia, Fabiola verfasserin aut Zambon, Alberto Andrea verfasserin aut Recupero, Salvatore verfasserin aut Fratini, Elena Sophia verfasserin aut Ciotti, Francesca verfasserin aut Fraschini, Maddalena verfasserin aut Sangalli, Mara verfasserin aut Sarzana, Marina verfasserin aut Clerici, Alessandra verfasserin aut Morena, Francesco verfasserin aut Martino, Sabata verfasserin aut Brooks, Jean verfasserin aut Richardson, Alan verfasserin aut Campbell, Laura verfasserin aut Aiuti, Alessandro verfasserin aut Fumagalli, Francesca verfasserin aut Enthalten in Molecular genetics and metabolism Orlando, Fla. : Academic Press, 1998 141 Online-Ressource (DE-627)268125260 (DE-600)1471393-7 (DE-576)106869493 1096-7206 nnns volume:141 GBV_USEFLAG_U GBV_ELV SYSFLAG_U SSG-OLC-PHA GBV_ILN_20 GBV_ILN_22 GBV_ILN_23 GBV_ILN_24 GBV_ILN_31 GBV_ILN_32 GBV_ILN_40 GBV_ILN_60 GBV_ILN_62 GBV_ILN_65 GBV_ILN_69 GBV_ILN_70 GBV_ILN_73 GBV_ILN_74 GBV_ILN_90 GBV_ILN_100 GBV_ILN_101 GBV_ILN_105 GBV_ILN_110 GBV_ILN_151 GBV_ILN_187 GBV_ILN_213 GBV_ILN_224 GBV_ILN_230 GBV_ILN_370 GBV_ILN_602 GBV_ILN_702 GBV_ILN_2001 GBV_ILN_2003 GBV_ILN_2004 GBV_ILN_2005 GBV_ILN_2007 GBV_ILN_2008 GBV_ILN_2009 GBV_ILN_2010 GBV_ILN_2011 GBV_ILN_2014 GBV_ILN_2015 GBV_ILN_2020 GBV_ILN_2021 GBV_ILN_2025 GBV_ILN_2026 GBV_ILN_2027 GBV_ILN_2034 GBV_ILN_2044 GBV_ILN_2048 GBV_ILN_2049 GBV_ILN_2050 GBV_ILN_2055 GBV_ILN_2056 GBV_ILN_2059 GBV_ILN_2061 GBV_ILN_2064 GBV_ILN_2088 GBV_ILN_2106 GBV_ILN_2110 GBV_ILN_2111 GBV_ILN_2112 GBV_ILN_2122 GBV_ILN_2129 GBV_ILN_2143 GBV_ILN_2152 GBV_ILN_2153 GBV_ILN_2190 GBV_ILN_2232 GBV_ILN_2336 GBV_ILN_2470 GBV_ILN_2507 GBV_ILN_4035 GBV_ILN_4037 GBV_ILN_4112 GBV_ILN_4125 GBV_ILN_4242 GBV_ILN_4249 GBV_ILN_4251 GBV_ILN_4305 GBV_ILN_4306 GBV_ILN_4307 GBV_ILN_4313 GBV_ILN_4322 GBV_ILN_4323 GBV_ILN_4324 GBV_ILN_4325 GBV_ILN_4326 GBV_ILN_4333 GBV_ILN_4334 GBV_ILN_4338 GBV_ILN_4393 GBV_ILN_4700 42.13 Molekularbiologie VZ 44.33 Physiologische Chemie VZ AR 141 |
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Gallo, Vera @@aut@@ Calbi, Valeria @@aut@@ De Mattia, Fabiola @@aut@@ Zambon, Alberto Andrea @@aut@@ Recupero, Salvatore @@aut@@ Fratini, Elena Sophia @@aut@@ Ciotti, Francesca @@aut@@ Fraschini, Maddalena @@aut@@ Sangalli, Mara @@aut@@ Sarzana, Marina @@aut@@ Clerici, Alessandra @@aut@@ Morena, Francesco @@aut@@ Martino, Sabata @@aut@@ Brooks, Jean @@aut@@ Richardson, Alan @@aut@@ Campbell, Laura @@aut@@ Aiuti, Alessandro @@aut@@ Fumagalli, Francesca @@aut@@ |
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Gallo, Vera Calbi, Valeria De Mattia, Fabiola Zambon, Alberto Andrea Recupero, Salvatore Fratini, Elena Sophia Ciotti, Francesca Fraschini, Maddalena Sangalli, Mara Sarzana, Marina Clerici, Alessandra Morena, Francesco Martino, Sabata Brooks, Jean Richardson, Alan Campbell, Laura Aiuti, Alessandro Fumagalli, Francesca |
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